Down-regulating α-synuclein for treating synucleopathies

Mov Disord. 2014 Oct;29(12):1463-5. doi: 10.1002/mds.26028. Epub 2014 Sep 12.
No abstract available

Keywords: Parkinson's disease; siRNA; therapeutic strategy; α-synuclein.

Publication types

  • Editorial
  • Research Support, Non-U.S. Gov't
  • Comment

MeSH terms

  • Animals
  • Brain / metabolism*
  • Gene Expression Regulation / drug effects*
  • Humans
  • Mutation / genetics*
  • RNA, Small Interfering / administration & dosage*
  • alpha-Synuclein / genetics*
  • alpha-Synuclein / metabolism*

Substances

  • RNA, Small Interfering
  • alpha-Synuclein